It was a chance of a lifetime, but it was scary for 10-year-old. Billy tells us about his memories and perspective being in a clinical trial for Duchenne Muscular Dystrophy. 

They were on the front lines of research that has now brought hope to some boys with Duchenne Muscular Dystrophy. Exon skipping clinical trial.

Cystic Fibrosis was a terminal disease when Nicole Horvath was born. She shouldn't be here. But she is, due to the research efforts of the Cystic Fibrosis Foundation.